I have found several news reports describing our discovery of our drug targets and a potential drug for Wolfram syndrome. These reports are written in lay terms and easy to understand. I appreciate these journalists help us raise awareness of Wolfram syndrome.
Thank you again for reading this. I am grateful.
Studying animal models and cells taken from patients with Wolfram syndrome, first author Simin Lu, PhD (left), and principal investigator Fumihiko Urano, MD, PhD, led a team that found the FDA-approved muscle relaxant dantrolene may be an effective treatment for the rare but devastating form of diabetes. Credit: Robert Boston