I always feel that we need to establish tight collaboration with pharmaceutical companies/biotechs to bring our new therapy and new therapeutic modality to our patients. They have expertise in making a crude drug into a real drug and going through the regulatory processes. I have spoken to many medical and scientific officers in industry to evangelize my idea, and I will keep on doing this. To accomplish this, I need to maintain the tight partnership with the patient organizations, my patients and their families. So please help me. I have three things always on my mind.
1. A cure for Wolfram syndrome
2. Provide better clinical care for Wolfram syndrome
3. Raise awareness of Wolfram syndrome
Thank you for reading this. I hope you have a wonderful day.