We clearly need drugs to stop the progression of Wolfram syndrome, so that we have time to develop stem cell-based therapies and gene therapies. Although we have discovered one drug that can potentially delay the progression of the disease, there is no guarantee this drug works. So I am building pipelines for the future. We are looking for novel drugs, testing combinations of different drugs, and developing novel drug screening methods.
Thank you for reading my blog today. I feel that something wonderful is going to happen to us soon. I am hopeful.