We have been developing drug-based therapies to delay/stop the progression of Wolfram Syndrome, and we have made significant progress. In parallel, we need to develop regenerative therapies to treat/replace damaged tissues. We have two pipelines for the regenerative therapies.
1. Stem cell-based therapies.
This requires collaboration with surgeons and bioengineers. We are working on this.
2. Regeneration factor-based therapies.
MANF and its receptors are our targets. We are making progress.
Regenerative Therapy Program should be set up in our hospital to bring these new therapies to our patients.We clearly have to go through regulatory processes. We need infrastructure to bring these therapies to our patients.
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