Our current focus is to bring a drug that can potentially delay the progression of the disease to our patients. In parallel, we are developing stem cell-based therapies and a new type of gene therapy.
A new type of gene therapy, CRISPR, is getting a lot of attention. We are also utilizing this technology. I have to say this is powerful and may change the future of medicine completely. This technology can correct gene mutations. Although no CRISPR-based drug exists, I have realized that there is a battle over the intellectual property rights for CRISPR. I hope this will be resolved soon, so that we can use this technology to help patients with genetic diseases.
Thank you for reading this blog. I feel hopeful today. I hope you have a wonderful weekend. I am thinking of you.