Month

January 2015

2 minutes done

I presented a 2 minute-pitch on the development of therapeutics for Wolfram syndrome yesterday. I did my best and had no regret. Stephanie Snow Gebel,... Read More

2 minutes today

As I mentioned before, I got a chance to present my work on the development of therapeutics for Wolfram syndrome in front of potential investors.... Read More

Speed up

I would like to speed up our progress. We are racing against time. If we can develop treatment for Wolfram, this can be applied to... Read More

Try and Try and Try again

I appreciate my teams’ multiple efforts to develop novel treatment for Wolfram syndrome. A dose-escalation study for dantrolene is ongoing. We are developing AAV-based gene... Read More