September 2014

Why am I optimistic?

I am optimistic because I see possibilities. We have FDA-approved drugs, new drugs, stem-cell therapies, and genome-editing therapies. When I came to Washington University Medical... Read More

Tipping the balance

I think about two S’s all the time, Small molecules (i.e., drugs) and Stem cell-based therapy. In Wolfram syndrome, there is imbalance of calcium levels... Read More

If we had…

Based on emails and phone calls from patients and their families, I am focusing my energy on the following three things. If we had these... Read More